Atsena Therapeutics
Gene therapy • Clinical-stage
Atsena Therapeutics is a clinical-stage gene therapy company focused on developing treatments for inherited retinal diseases such as X-linked retinoschisis and Leber congenital amaurosis type 1.
Axonis Therapeutics
Biotechnology • Neuromedicines
Axonis Therapeutics is a biotechnology company developing novel neuromedicines targeting neurological disorders like epilepsy and pain.